Study detail
Recruiting
A Retrospective Cohort Study to Characterize Propionic Acidemia Patients
ModernaTX, Inc.
Summary
This is a non-interventional, observational, global, multicenter, study describing participant characteristics, clinical outcomes, and event rates in participants with propionic acidemia (PA).
Description
Data will be abstracted through medical record review ensuring inclusion only of data from participants meeting all the inclusion criteria and none of the censoring criteria. Data will be collected retrospectively from study sites, including medical clinics, hospitals and academic medical centers.
Eligibility
- Age range
- 2+ years
- Sex
- All
- Healthy volunteers
- No
Detailed criteria