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A Multi-Center, Prospective, Longitudinal, Study Evaluating Immunologic, Inflammatory, and Laboratory Parameters Associated With Long-Term Palynziq® (Pegvaliase) Treatment in Subjects With Phenylketonuria (PKU) in the United States
This is a 10-year multi-center, prospective, longitudinal, single arm study evaluating immunologic, inflammatory and laboratory parameters associated with long…
Phenylketonuria (PKU)
BioMarin PharmaceuticalNCT06305234
Phase 3
An Open-Label Study to Evaluate the Long-Term Safety of JNT-517 in Participants With Phenylketonuria
The goal of this Phase 3, open-label study is to evaluate the long-term safety of JNT-517 in pediatric and adult participants with Phenylketonuria (PKU) after …
Phenylketonuria (PKU)
Otsuka Pharmaceutical Development & Commercialization, Inc.NCT06628128
Phase 2
A Phase 2 Study of JNT-517 in Adolescent Participants With Phenylketonuria
The goal of this Phase 2, randomized study is to assess the safety, tolerability, and pharmacokinetics (PK) of oral JNT-517 in adolescents (12 to less than 18 …
Phenylketonuria (PKU)
Otsuka Pharmaceutical Development & Commercialization, Inc.NCT06637514
A Multi-Center, Observational Study to Evaluate the Long-Term Safety of Subcutaneous Injections of Palynziq® (Pegvaliase) in Subjects With Phenylketonuria
This is a 10-year multi-center, global, observational study to further characterize the safety profile of pegvaliase, including hypersensitivity reactions, lon…
Phenylketonuria (PKU)
BioMarin PharmaceuticalNCT05813678