Duchenne Muscular Dystrophy Quality of Life: Qualitative Interviews With Patients and Caregivers
Red Nucleus Enterprise Solutions, LLC
Summary
The purpose of this study is to understand DMD functional losses or abilities and their association with independence and quality of life from the perspective of individuals with DMD and/or and their caregivers. This is a qualitative interview study in which individuals with DMD and/or their caregivers will be asked to participate in a semi-structured, approximately 60- minute interview. Interviews will focus on functional abilities and independence. Caregivers and boys with DMD will be interviewed. This study includes no treatment nor intervention; however, some participants are being treated by a drug that is approved in the U.S. and the U.K. and under investigation in other geographies.
Eligibility
- Age range
- 10+ years
- Sex
- Male
- Healthy volunteers
- No
Inclusion Criteria: Subsample A - Patients Eligible participants for Subsample A must: * Have been treated with Givinostat for at least 2 years * Be at least 10 years of age with signed consent of a parent or legal guardian * Be currently taking givinostat * Willing and able to participate in a video and/or audio recorded interview Subsample A - Caregivers Eligible caregivers for Subsample A must: * Be a parent or legal guardian of an individual with DMD that has been taking givinostat for at least two years * Willing and able to participate in a video and/or audio recorded interview Su…
Location
- Red NucleusYardley, Pennsylvania