Treatment Patterns, Biochemical Profiles and Clinical Outcomes in Adults With X-Linked Hypophosphatemia - A Prospective Observational Cohort Study - IBIS XLH
Novo Nordisk A/S
Summary
The purpose of this study is to better understand how X-linked hypophosphatemia (XLH) affects the body and daily life. Phosphate levels are critical in managing XLH, we aim to study how these levels change in patients taking burosumab and how they relate to bone health, overall disease burden and XLH-related conditions.
Eligibility
- Age range
- 18–64 years
- Sex
- All
- Healthy volunteers
- No
Inclusion Criteria: * Informed consent obtained before any trial-related activities, i.e., any procedure related to recording of data according to the protocol. * Male or female and aged 18-64 years (both inclusive) at the time of signing informed consent. * Diagnosis of congenital XLH, confirmed genetically or clinically as determined by the investigator, supported by documentation. * Participants have been treated with burosumab for at least 90 days prior to the screening/baseline visit and treatment is still ongoing. * Participant confirms ability and willingness to attend visits according…