This study will collect information from patients with Alagille syndrome (ALGS) as they use odevixibat (Bylvay) in their daily lives. Odevixibat is a medicine…

Alagille Syndrome

~Estimated

~$10 – $1,125

IpsenNCT06850038

Coordination of Rare Diseases at Sanford

CoRDS, or the Coordination of Rare Diseases at Sanford, is based at Sanford Research in Sioux Falls, South Dakota. It provides researchers with a centralized, …

Rare DisordersUndiagnosed DisordersDisorders of Unknown Prevalence+340 more

Long-Term SafEty and Clinical Outcomes of LivmArli in Patients in the United States (LEAP-US)

The objective of this 5-year, prospective, observational cohort study is to evaluate the long-term safety and clinical outcomes of patients with Alagille syndr…

Alagille SyndromeProgressive Familial Intrahepatic Cholestasis

~Estimated

~$10 – $1,050

Mirum Pharmaceuticals, Inc.NCT06193928

~Estimated

~$10 – $1,125

Sanford HealthNCT01793168