The aim of this registry to understand the natural history and disease progression in ALD and potentially develop bio-markers using the biospecimens collected …

ALD (Adrenoleukodystrophy)AdrenoleukodystrophyCerebral Adrenoleukodystrophy

~Estimated

~$10 – $750

Masonic Cancer Center, University of MinnesotaNCT03789721

A Postmarketing, Prospective, Multicenter, Observational, Long-Term Safety and Effectiveness Registry Study of Patients With Cerebral Adrenoleukodystrophy (CALD) Treated With Elivaldogene Autotemcel (Stargazer)

The main aim of this study is to assess and describe the safety outcomes, including newly diagnosed malignancies, of patients with CALD treated with eli-cel in…

Cerebral Adrenoleukodystrophy (CALD)

~Estimated

~$10 – $1,050

Genetix Biotherapeutics Inc.NCT06224413