Browse studies

Find your next paid study

5 recruiting studies matching your filters

Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension

This is a natural history study to improve the types of assessments and biological samples that will be used in clinical drug trials in both congenital myotoni…

Congenital Myotonic DystrophyChildhood Myotonic DystrophyMyotonic Dystrophy

Estimated

~$10 – $750

Virginia Commonwealth UniversityNCT06747884

Assessing Pediatric Endpoints in DM1 (ASPIRE-DM1)

The overall goal of the study is to establish valid clinical endpoint assessments for children with congenital myotonic dystrophy type 1 and develop biomarkers…

Congenital Myotonic DystrophyCDM

Estimated

~$10 – $750

Virginia Commonwealth UniversityNCT05224778

National Registry of Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Patients and Family Members

Myotonic dystrophy (DM) and facioscapulohumeral muscular dystrophy (FSHD) are inherited disorders characterized by progressive muscle weakness and loss of musc…

Myotonic DystrophyFacioscapulohumeral Muscular DystrophyMuscular Dystrophy+6 more

Estimated

~$10 – $750

University of RochesterNCT00082108

Phase 2

An Open-Label Study to Evaluate the Long-Term Safety and Efficacy of Tideglusib for the Treatment of Congenital or Childhood Onset DM1 (REACH CDM X)

This is an open-label phase 2/3 study for individuals with Congenital Myotonic Dystrophy (Congenital DM1) who participated in the preceding AMO-02-MD-2-003 stu…

Congenital Myotonic Dystrophy

Estimated

~$10 – $8,750

AMO Pharma LimitedNCT05004129

Myotonic Dystrophy Family Registry

The Myotonic Dystrophy Family Registry (MDFR) is an online, patient-entered database that collects information on myotonic dystrophy (DM) to aid researchers in…

Myotonic DystrophyCongenital Myotonic DystrophyMyotonic Dystrophy 1+13 more

Estimated

~$10 – $750

Myotonic Dystrophy FoundationNCT02398786