Browse studies
Find your next paid study
3 recruiting studies matching your filters
A Long-term Follow-up Study in Patients With Hemoglobinopathy Who Received Autologous CD34+ Edited Hematopoietic Stem Cells
This is a Long-term Follow-up (LTFU) study in patients who received BEAM-101 in the parent study (Study BTX-AUT-001). Eligible patients who received BEAM-101 w…
HemoglobinopathySickle Cell Disease
Beam Therapeutics Inc.NCT07373639
Phase 1
Determination of Red Cell Survival in Sickle Cell Disease and Other Hemoglobinopathies Using Biotin Labeling
Background: Sickle cell disease (SCD) is an inherited disorder of the blood. SCD causes red blood cells (RBCs) to die early. This can lead to a shortage of he…
Sickle Cell DiseaseThalassemiaHemoglobinopathy
National Heart, Lung, and Blood Institute (NHLBI)NCT06313398
Phase 2
Study of TCR Alpha Beta T-Cell and CD19 B-Cell Depletion for Hematopoietic Cell Transplantation From Haploidentical Donors in the Treatment of Non-Malignant Hematological Disorders in Children
This research is being done to learn if a new type of haploidentical transplantation using TCR alpha beta and CD19 depleted stem cell graft from the donor is s…
Hemoglobinopathy (Disorder)Severe Aplastic AnemiaBone Marrow Failure Syndrome
Johns Hopkins All Children's HospitalNCT04356469