Browse studies
Find your next paid study
2 recruiting studies matching your filters
Mucopolysaccharidosis VII Disease Monitoring Program (MPS VII DMP)
The objectives of this study are to characterize MPS VII disease presentation and progression and assess long-term effectiveness and safety, including hypersen…
Mucopolysaccharidosis VIIMPS VIIMPS 7+1 more
Estimated
~$10 – $1,050
Ultragenyx Pharmaceutical IncNCT03604835
Phase 1
PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)
For detailed information, please view our study website: https://pearltrial.ucsf.edu/ The investigators aims to determine the the maternal and fetal safety an…
MPS IMPS IIMPS IVA+6 more
Estimated
~$10 – $5,625
University of California, San FranciscoNCT04532047