Browse Studies — Arctuva

Molecular Analysis of Neuromuscular Disease

In the Congenital Myopathy Research Program at Boston Children's Hospital and Harvard Medical School, the researchers are studying the congenital myopathies (n…

Central Core DiseaseCentronuclear MyopathyCongenital Fiber Type Disproportion+5 more

Estimated

~$10 – $750

Boston Children's HospitalNCT00272883

Observational

Dilated Cardiomyopathy Detection Using Artificial Intelligence and Screening With Mobile Technology

This is a prospective, single-arm clinical trial in which participants with dilated cardiomyopathy will invite their first degree relatives to undergo mobile c…

Dilated CardiomyopathyHeart FailureHeart Disease

Estimated

~$10 – $6,250

Lancaster General HospitalNCT06688396

Real-World Camzyos Patient Reported OutcoMes Through PAtient SurveyS in Hypertrophic CardioMyopathy (COMPASS-HCM): A Prospective Longitudinal Study

This real-world study will assess changes in health status among participants with symptomatic obstructive hypertrophic cardiomyopathy who are treated with mav…

Obstructive Hypertrophic Cardiomyopathy

Estimated

~$10 – $1,125

Bristol-Myers SquibbNCT06551129

Phase 1

A Phase 1 Dose Escalation Trial Evaluating an Intravenously Administered Recombinant Adeno-Associated Virus Serotype rh.74 (AAVrh.74) Vector Containing the Human Plakophilin-2a (PKP2a) Coding Sequence (RP-A601; AAVrh.74-PKP2a) in Subjects With Arrhythmogenic Cardiomyopathy Arising From Pathogenic PKP2 Variants (PKP2-ACM)

This Phase 1 dose escalation trial will assess the safety and preliminary efficacy of a single dose intravenous infusion of RP-A601 in high-risk adult patients…

PKP2 Arrhythmogenic Cardiomyopathy (PKP2-ACM)

Estimated

~$10 – $8,750

Rocket Pharmaceuticals Inc.NCT05885412