Browse Studies — Arctuva

Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension

Myotonic Dystrophy type 1 (DM1) is an autosomal dominant multisystemic disorder that causes progressive disability and shortened life expectancy. It is charact…

DM1Myotonic DystrophyMyotonic Dystrophy 1+4 more

Estimated

~$10 – $750

Virginia Commonwealth UniversityNCT07700225

Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)

Building on previous work of the Myotonic Dystrophy Clinical Research Network (DMCRN), the present study seeks to overcome insufficient data on natural history…

Myotonic Dystrophy 1DM1

Estimated

~$10 – $750

Virginia Commonwealth UniversityNCT03981575

Phase 1

A Phase 1/2a Double-Blind, Placebo-controlled, Single- and Multiple Ascending Dose Study to Assess the Safety, Tolerability, PK, PD and Efficacy of IV Administration of ATX-01 In Male and Female Participants Aged 18 to 64 With Classic DM1

The goal of this clinical trial is to test ATX-01 in participants with myotonic dystrophy type 1 (DM1). The main question it aims to answer is if ATX-01 is saf…

Myotonic Dystrophy 1

Estimated

~$10 – $8,750

ARTHEx Biotech S.L.NCT06300307

Myotonic Dystrophy Family Registry

The Myotonic Dystrophy Family Registry (MDFR) is an online, patient-entered database that collects information on myotonic dystrophy (DM) to aid researchers in…

Myotonic DystrophyCongenital Myotonic DystrophyMyotonic Dystrophy 1+13 more

Estimated

~$10 – $750

Myotonic Dystrophy FoundationNCT02398786