The objective of this project is to develop a Neurogenetics patient database and bio repository - which includes clinical information regarding history, physic…

Neurogenetic Disorders

~Estimated

~$10 – $750

University of PittsburghNCT02995538

Phase 1

Safety and Efficacy of AAV9/AP4B1 For Patients With AP4B1-related Hereditary Spastic Paraplegia Type 47 (SPG47): A Phase 1/2 Single-Center, Open-Label Study of Stereotactic Intra-cisterna Magna Administration

Safety and Efficacy of AAV9/AP4B1 For Patients with AP4B1-related Hereditary Spastic Paraplegia Type 47 (SPG47): A Phase 1/2 Single-Center, Open-Label Study of…

HSPHereditary Spastic ParaplegiaHereditary Spastic Paraparesis+10 more

~Estimated

~$10 – $8,750

BlackfinBio LtdNCT06948019