The goal of this clinical trial is to learn if a gene therapy called scAAV9.CB.CLN6 can treat children with CLN6 Batten disease (variant late infantile neurona…

CLN6Batten DiseaseBatten's Disease+2 more

~Estimated

~$10 – $6,250

The Charlotte and Gwenyth Gray FoundationNCT07582484

Clinical and Neuropsychological Investigations in Batten Disease

This study aims to assess the natural history of Batten disease (Neuronal Ceroid Lipofuscinosis) by obtaining information about the motor, behavioral, and func…

Neuronal Ceroid LipofuscinosisNeuronal Ceroid Lipofuscinosis CLN1Neuronal Ceroid Lipofuscinosis CLN2+7 more

~Estimated

~$10 – $750

University of RochesterNCT01873924