Browse studies
Find your next paid study
16 recruiting studies matching your filters
Phase 2
A Phase 2 Study of JNT-517 in Adolescent Participants With Phenylketonuria
The goal of this Phase 2, randomized study is to assess the safety, tolerability, and pharmacokinetics (PK) of oral JNT-517 in adolescents (12 to less than 18 …
Phenylketonuria (PKU)
Estimated
~$10 – $8,750
Otsuka Pharmaceutical Development & Commercialization, Inc.NCT06637514
A Global, Multicenter Study to Assess Maternal, Fetal and Infant Outcomes of Exposure to Palynziq® (Pegvaliase) During Pregnancy and Breastfeeding
This is a Phase 4 observational study designed to assess the impact of Palynziq ® (pegvaliase) treatment in pregnant women with PKU and on their offspring who …
Phenylketonuria, Maternal
Estimated
~$10 – $1,050
BioMarin PharmaceuticalNCT05579548
Observational
Educational, Social Support, and Nutritional Interventions and Their Cumulative Effect on Pregnancy Outcomes and Quality of Life in Teen and Adult Women With Phenylketonuria (PKU) or Maple Syrup Urine Disease (MSUD).
The purpose of this project is to study the effectiveness of teaching teens and young women with Phenylketonuria (PKU) or Maple Syrup Urine Disease (MSUD) abou…
PregnancyPhenylketonuria
Estimated
~$10 – $6,250
Emory UniversityNCT01659749
A Multi-Center, Observational Study to Evaluate the Long-Term Safety of Subcutaneous Injections of Palynziq® (Pegvaliase) in Subjects With Phenylketonuria
This is a 10-year multi-center, global, observational study to further characterize the safety profile of pegvaliase, including hypersensitivity reactions, lon…
Phenylketonuria (PKU)
Estimated
~$10 – $1,050
BioMarin PharmaceuticalNCT05813678