This is a Phase 1/2, open-label, multiple-center, dose escalation and cohort expansion study to evaluate the safety and efficacy of NGGT002 in adult subjects w…

Phenylketonurias

~Estimated

~$10 – $8,750

NGGT INC.NCT06332807

Palynziq and PKU: Treatment Impacts on Diet Quality, Neurological Health, Nutritional Status, and the Metabolome

Phenylketonuria (PKU) is an inherited metabolic disorder that impairs the metabolism of the essential amino acid phenylalanine (Phe). Without stringent dietary…

Phenylketonurias

~Estimated

~$10 – $750

Emory UniversityNCT04404530

Observational

Development of Novel Psychological Assessment Tools and Anxiety Intervention for PKU: Intervention Trial

While previous PKU intervention research has largely focused on pharmacological treatment of elevated Phe levels, the adaptation of evidence-based psychosocial…

Phenylketonurias

~Estimated

~$10 – $6,250

University of Missouri-ColumbiaNCT06560736