Given the expansion of indications for genetic testing and our understanding of conditions for which the results change medical management, it is imperative to…

Genetic PredispositionParagangliomaPheochromocytoma+7 more

~Estimated

~$10 – $6,250

University of PennsylvaniaNCT06377033

Phase 3

A Phase 3, Randomized, Multicenter, Double-Blind, Placebo-Controlled Study of Acoramidis for Transthyretin Amyloidosis Prevention in the Young (ACT-EARLY Trial)

Transthyretin amyloidosis (ATTR) is a disease where the normally occurring transthyretin (TTR) protein falls apart and forms amyloid, a sticky plaque-like subs…

AmyloidosisAmyloid CardiomyopathyTransthyretin Amyloidosis+3 more

~Estimated

~$10 – $8,750

Eidos Therapeutics, a BridgeBio companyNCT06563895