3 recruiting studies matching your filters
PROSPECT is a prospective observational registry and longitudinal natural history study of adults at risk for genetic prion disease.
The purpose of this trial is to evaluate safety, tolerability, pharmacokinetics and pharmacodynamic impact of PrP-siRNA in symptomatic prion disease patients.
We are doing this research to identify biomarkers in individuals who are at-risk for familial prion disease. We hope to use these biomarkers to predict timing …