This is a REMOTE prospective observational study of participants with MPS IIIC. No investigational medicinal product will be administered as part of this stud…

Sanfilippo Syndrome Type CMucopolysaccharidosis (MPS) IIIC

~Estimated

~$10 – $1,125

Phoenix NestNCT07712003

A Combination Retrospective and Prospective Natural History Study of Participants With Sanfilippo Syndrome Mucopolysaccharidosis Type IIIC (MPS IIIC)

This study is planned to document, through retrospective and prospective data collection, syndrome progression in children and young adults with MPS IIIC.

Sanfilippo Syndrome Type C

~Estimated

~$10 – $1,125

Phoenix NestNCT05825131