Browse Studies — Arctuva

Phase 3

A Pivotal, Parallel-Arm, Phase 3, Open-Label, Active-controlled, Global, Multicenter, Randomized Basket Trial Investigating the Efficacy and Safety of Once-weekly Lonapegsomatropin Compared to Daily Somatropin in Prepubertal Children and Adolescents With Growth Failure or Short Stature Due to Growth Hormone Sufficient Disorders - Turner Syndrome, SHOX Deficiency, Small for Gestational Age, and Idiopathic Short Stature

This basket trial will enroll prepubertal children and adolescents with clinically diagnosed and genetically confirmed (if applicable) TS, SHOX-D, SGA, or ISS …

Turner SyndromeShort Stature Homeobox Gene MutationIdiopathic Short Stature+1 more

Estimated

~$10 – $8,750

Ascendis Pharma A/SNCT07221851

A Multicenter, Observational Study to Characterize Growth in Children With Idiopathic Short Stature

Study 111-903 will generate baseline growth data in children with ISS by collecting growth measurements and other variables of interest.

Idiopathic Short Stature

Estimated

~$10 – $1,050

BioMarin PharmaceuticalNCT06309979

Phase 2

A Phase 2, Randomized, Controlled, Multicenter Study of Vosoritide in Children With Idiopathic Short Stature

The purpose of this study is to evaluate i) the effect of multiple doses of vosoritide and ii) the effect of the therapeutic dose of vosoritide compared to hum…

Idiopathic Short Stature

Estimated

~$10 – $8,750

BioMarin PharmaceuticalNCT06382155

Phase 2

Vosoritide for Treatment of Short Stature in Girls With Turner Syndrome

Turner syndrome (TS) is characterized by a missing whole or part of the second sex chromosome in a phenotypic female, resulting in short stature due to haploin…

Turner SyndromeShort Stature

Estimated

~$10 – $7,500

Roopa Kanakatti Shankar, MBBS, MSNCT05849389