The purpose of the study is to assess the efficacy, safety, and tolerability of zeleciment basivarsen (DYNE-101) for the treatment of myotonic dystrophy 1 (DM1…

Myotonic Dystrophy Type 1 (DM1)DM1Myotonic Dystrophy+2 more

~Estimated

~$10 – $8,750

Dyne TherapeuticsNCT07486934

National Registry of Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Patients and Family Members

Myotonic dystrophy (DM) and facioscapulohumeral muscular dystrophy (FSHD) are inherited disorders characterized by progressive muscle weakness and loss of musc…

Myotonic DystrophyFacioscapulohumeral Muscular DystrophyMuscular Dystrophy+6 more

~Estimated

~$10 – $750

University of RochesterNCT00082108

Myotonic Dystrophy Family Registry

The Myotonic Dystrophy Family Registry (MDFR) is an online, patient-entered database that collects information on myotonic dystrophy (DM) to aid researchers in…

Myotonic DystrophyCongenital Myotonic DystrophyMyotonic Dystrophy 1+13 more

~Estimated

~$10 – $750

Myotonic Dystrophy FoundationNCT02398786