XLMTM (X-linked myotubular myopathy) is a serious genetic muscle condition. It is caused by changes in the MTM1 gene which stops or slows down normal muscle de…

X-Linked Myotubular Myopathy

~Estimated

~$10 – $1,125

Astellas Gene TherapiesNCT06581146

Phase 1

A Phase 1/2, Multicenter, Open-label, Dose Escalation and Expansion Clinical Study to Evaluate the Safety, Tolerability and Preliminary Efficacy of ASP2957 in Male Participants With Invasive Ventilator-dependent X-linked Myotubular Myopathy

X-linked myotubular myopathy (XLMTM) is a rare and serious condition present at birth where the muscles do not work properly. There are currently no approved t…

X-Linked Myotubular Myopathy

~Estimated

~$10 – $7,500

Astellas Gene TherapiesNCT07052929